Genetic Rx
Date: Location: Cost:
December 7, 2017 Harvard Medical School - Joseph B. Martin Conference Center
77 Avenue Louis Pasteur
Boston, MA 02115
(617) 262-9600
Location >

Starting at $1950


Dress Code:
Business Attire


Genetic Rx - December 7, 2017 - DRAFT

Co-hosts: Tom Barnes, Louis Breton, Jim Burns, Geoff MacKay, Sandy Macrae, Sue Washer

Time Agenda
8:00-9:00 am

Registration and Networking Breakfast

9:00-9:15 am

Welcome and Opening Remarks

9:15-9:45 am

Gene Therapy: New Therapeutic Modalities
Walter Strapps, VP Discovery, Intellia Therapeutics

9:45-10:15 am

Gene Editing: Progress to the Clinic
Michael Dombeck, VP, Business Development, Precision Biosciences; Michael Maguire, CEO, Avectas

10:15-10:45 am

Next Generation RNA Technologies
Joseph Payne, Founder, President & CEO, Arcturus Therapeutics
Moderator: Edward Kaye, CEO, Stoke Therapeutics

10:45-11:15 am

Networking Break

11:15-11:45 am

Patient Recruitment and Engagement

11:45-12:15 pm

Manufacturing and Commercialization: Strategies for Success
Geoff MacKay, President & CEO, AvroBio; Alexander White, Head Agility & Rare Disease Commercialization, Roche
Moderator: Sue Washer, President & CEO, AGTC

12:15-1:15 pm

Networking Lunch

1:15-1:45 pm

Moving Beyond Rare Diseases: What are the Challenges?
PJ Brooks, Program Director Office of Rare Diseases Research & Division of Clinical Innovation, NIH; Anne Marie Finley, President, Biotech Policy Group; Jeff Galvin, CEO, American Gene Technologies

1:45-2:15 pm

Genetic Approaches to Hemophilia
Edward Kaye, CEO, Stoke Therapeutics
Moderator: Greg LaRosa, SVP & CSO, Rare Disease Research Unit, Pfizer

2:15-2:45 pm

Academia, Industry, & Venture Partnerships: The New Wave
Gregory Robinson
, Chief Scientific Officer, Nightstar Therapeutics
Moderator: Nora Yang, Director, Portfolio Management & Strategic Operations, NIH

2:45-3:15 pm

Moderated Keynote

3:15-3:45 pm

Networking Break

3:45-4:15 pm

Regulatory Strategies for Gene Therapy Products
John Maslowski, President & CEO, Fibrocell Science; Jennifer Spinella, EVP, Regulatory Affairs & Quality Assurance, Renova Therapeutics
Moderator: Jack Reich, CEO & Co-Founder, Renova Therapeutics

4:15-4:45 pm

Defining the Value of Genetic Therapies
Louis Breton
, Co-Founder & CEO, Calimmune

4:45-5:15 pm

Attracting Investment into the Field

5:15-5:45 pm

Industry Outlook for 2018: What Will the Key Drivers Be?

5:45-5:55 pm

Presentation of the Innovation of the Year Award

5:55-6:40 pm

Cocktails and Hors d'oeuvres

Supporting Sponsors: (see all sponsors)