Genetic Rx
Date: Location: Cost:
December 7, 2017 Harvard Medical School - Joseph B. Martin Conference Center
77 Avenue Louis Pasteur
Boston, MA 02115
(617) 262-9600
Location >

Starting at $1950


Dress Code:
Business Attire


Genetic Rx - December 7, 2017 - DRAFT

Co-hosts: Tom Barnes, Louis Breton, Jim Burns, Geoff MacKay, Sandy Macrae, Sue Washer

Time Agenda
7:00-8:00 am

Registration and Networking Breakfast

8:00-8:15 am

Welcome and Opening Remarks

8:15-8:45 am

Gene Therapy: New Therapeutic Modalities
Tom Barnes, CSO, Intellia Therapeutics

8:45-9:15 am

Gene Editing: Progress to the Clinic
Jim Burns, President & CEO, Casebia Therapeutics; Michael Dombeck, VP, Business Development, Precision Biosciences; Sandy Macrae, President & CEO, Sangamo Therapeutics; Michael Maguire, CEO, Avectas

9:15-9:45 am

Epigenetics: The Future of Genetic Modification

9:45-10:15 am

Next Generation RNA Technologies
Joseph Payne, Founder, President & CEO, Arcturus Therapeutics
Moderator: Edward KayePresident, CEO & CMO, Sarepta Therapeutics

10:15-10:45 am

Networking Break

10:45-11:15 am

The First Step to Finding a Cure: Diagnostics

11:15-11:45 am

Patient Recruitment and Engagement

11:45-12:15 pm

Manufacturing and Commercialization: Strategies for Success
Geoff MacKay, President & CEO, AvroBio
Moderator: Sue Washer, President and CEO, AGTC

12:15-1:15 pm

Networking Lunch

1:15-1:45 pm

Moving Beyond Rare Diseases: What are the Challenges?
PJ BrooksProgram Director, NIH; Anne Marie Finley, President, Biotech Policy Group

1:45-2:15 pm

Genetic Approaches to Hemophilia
Edward KayePresident, CEO & CMO, Sarepta
Moderator: Greg LaRosa, SVP and CSO, Rare Disease Research Unit, Pfizer

2:15-2:45 pm

Academia, Industry, & Venture Partnerships: The New Wave

2:45-3:05 pm

Fireside Chat

3:05-3:30 pm

Networking Break

3:30-4:00 pm

Regulatory Strategies for Gene Therapy Products
John Maslowski, President and Chief Executive Officer, Fibrocell
Moderator: Jack Reich, CEO & Co-Founder, Renova Therapeutics

4:00-4:30 pm

Defining the Value of Genetic Therapies
Louis Breton, CEO & Co-Founder, Calimmune

4:30-5:00 pm

Attracting Investment into the Field

5:00-5:30 pm

Industry Outlook for 2018: What Will the Key Drivers Be?

5:30-5:40 pm

Presentation of the Innovation of the Year Award

5:40-6:30 pm

Cocktails and Hors d'oeuvres

Supporting Sponsors: (see all sponsors)